Contact the staff listed below for more information about the NCATS Division of Rare Diseases Research Innovation.
General contact information: (301) 435-0916 or NCATS Division of Rare Diseases Research Innovation.
Stay connected with the Division of Rare Diseases Research Innovation on Facebook and Twitter.
|
Area of Expertise |
Contact |
Phone Number |
|---|---|---|
|
Program Director: Alice Chen Grady, M.D. |
(301) 827-2015 |
|
|
Program Director: Eric Sid, M.D., M.H.A. Program Administrator: Jim Dickens |
(301) 827-3073 (301) 827-9507 |
|
|
Genetic Therapies, General |
Program Director: Philip John (P.J.) Brooks, Ph.D. Program Administrator: Deanna Portero |
(301) 443-0513
(301) 451-9968 |
|
Program Director: Eric Sid, M.D., M.H.A. |
(301) 827-3073 |
|
|
Program Director: Alice Chen Grady, M.D. |
(301) 827-2015 |
|
| NCATS Toolkit for Patient-Focused Therapy Development (Toolkit) |
Program Director: Eric Sid, M.D., M.H.A. Program Administrator: Jim Dickens |
(301) 827-3073 (301) 827-9507 |
|
Non-Viral Technologies for in vivo Delivery of Genome Editors |
Program Director: Philip John (P.J.) Brooks, Ph.D. |
(301) 443-0513 |
|
Program Director: Tiina Urv, Ph.D. Program Administrator: Joanne Lumsden, Ph.D. |
(301) 827-2746 (301) 443-3676 |
|
|
Program Director: Tiina Urv, Ph.D. Program Administrator: Joanne Lumsden, Ph.D. |
(301) 827-2746 (301) 443-3676 |
|
|
Program Director: Alice Chen Grady, M.D. Program Administrator: Meera Shah, M.P.H. |
(301) 827-2015 (301) 827-6222 |
|
|
Program Director: Eric Sid, M.D., M.H.A. Program Administrator: Jim Dickens
|
(301) 827-3073 (301) 827-9507 |
|
|
Program Director: Philip John (P.J.) Brooks, Ph.D. Program Administrator: Deanna Portero
|
(301) 443-0513
(301) 451-9968 |
|
|
Trans-NIH Rare Diseases Working Group |
Program Director: Tiina Urv, Ph.D. Program Administrator: Meera Shah, M.P.H. |
(301) 827-2746 (301) 827-6222 |
|
All Other Inquiries |
Program Administrator: Tierra Clarke |
(301) 435-0916 |
Visit our rare disease research programs:
- The Genetic and Rare Diseases (GARD) Information Center provides up-to-date health information about numerous rare and genetic diseases.
- The Rare Diseases Registry Program (RaDaR), formerly known as the Global Rare Diseases Registry Data Repository program, aims to define best practices for patient registries. RaDaR also strives to identify and adopt standards to support high-quality registries for rare diseases therapeutics development.
- The Rare Diseases Clinical Research Network (RDCRN) is designed to advance medical research on rare diseases by providing support for clinical studies and facilitating collaboration, study enrollment and data sharing.
- The NCATS Toolkit for Patient-Focused Therapy Development is a collection of online resources that can help patient groups advance through the process of therapy development.
- The Clinical Trial Readiness for Rare Diseases, Disorders and Syndromes (CTR) grants program supports projects focused on collecting the data needed to move promising rare disease therapies and diagnostics to clinical trial.
- The Platform Vector Gene Therapy (PaVe-GT) pilot project will test whether it is possible to increase the efficiency of gene therapy clinical trial startup by using the same gene delivery system and manufacturing methods for multiple gene therapies.