Cyclodextrins as Therapeutics for Lysosomal Storage Disorders
Lead Inventor: Wei Zheng (NCATS)
Inventors: Juan Marugan (NCATS), John McKew (NCATS), Manju Swaroop (NHGRI), Miao Xu (NHGRI)
Ref. No.: E-050-2012/0
Abstract: Cyclodextrins, alone or in combination with other agents (e.g., vitamin E), as therapeutics for the treatment of lysosomal storage disorders caused by the accumulation of non-cholesterol lipids.
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