News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
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Paving the Way for Ultrarare Bone Disease Treatment Trial
May 21, 2024 - NCATS News
- Our Impact on Drug Discovery and Development
- Therapeutics for Rare and Neglected Diseases (TRND)
Clinicians at the NIH Clinical Center will soon start testing an investigative drug for an ultrarare bone disease.
Read ArticleEveryLife Foundation Announces Scientific Workshop on ‘Ultra-Rare’ Diseases
May 16, 2024 - Media Coverage
- Our Impact on Rare Diseases
Communicating About Rare Diseases
February 28, 2024 - NCATS News
- Our Impact on Rare Diseases
NCATS Director Joni Rutter penned a guest post for NIH’s Science, Health, and Public Trust blog on why communicating about rare diseases research is important and what to consider when sharing info
Breaking Down Prednisone Too Quickly May Short-Circuit Its Benefit for Rare Neuromuscular Disorder
February 15, 2024 - NCATS News
- Rare Diseases Clinical Research Network (RDCRN)
Chemicals produced when the body breaks down the drug prednisone could indicate which patients with a rare muscle disorder were helped by the drug.
Global Patient Registries Can Advance Opportunities for Rare Disease Research
December 14, 2023 - Media Coverage
- Rare Diseases Registry Program (RaDaR)
Rare Syndrome After COVID Vaccines Described
December 3, 2023 - Media Coverage
- Clinical and Translational Science Awards (CTSA) Program
Newborn Screening for Rare Immune Disorders Led to Earlier Treatment, Improved Survival
November 20, 2023 - NCATS News
- Rare Diseases Clinical Research Network (RDCRN)
An NCATS-led Rare Diseases Clinical Research Network consortium changed what is known about severe combined immunodeficiency.
Pushing for Better Clinical Trial Design for Rare Diseases
October 17, 2023 - Grantee/Partner News