News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
NIH, AlphaRose Study Advances Personalised Therapy Approach for Rare Genetic Disorder
July 16, 2026 - Media Coverage
- Our Impact on Drug Discovery and Development
- Our Impact on Rare Diseases
FDA OKs First-in-Human Trial for BGTC-Supported Rare Disease Gene Therapy
July 7, 2026 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Cures Within Reach Selected Three Clinical Trials in Rare/Ultra-Rare Diseases to Validate AI Predictions
February 25, 2026 - Grantee/Partner News
- Biomedical Data Translator (Translator)
Children’s Hospital of Philadelphia Marks One-Year Anniversary of World’s First Personalized CRISPR Gene Therapy for Child with Rare Genetic Disease
February 24, 2026 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
New Initiative Aims to Revive Stalled Rare Disease Therapies
February 24, 2026 - Media Coverage
- Our Impact on Rare Diseases
More Than 30 Million Americans Living With Rare Diseases
February 23, 2026 - Grantee/Partner News
- Clinical and Translational Science Awards (CTSA) Program
Rare Diseases Clinical Research Network Awardees Expand the Reach of NIH Impact
February 5, 2026 - NCATS News
- Rare Diseases Clinical Research Network (RDCRN)
NIH awarded funding to 10 new and five continuing Rare Diseases Clinical Research Network (RDCRN) consortia to help address challenges in rare diseases treatment development.
UNC Researchers Awarded $7.3 Million to Advance Research on Rare Bronchiectatic Diseases
February 4, 2026 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)