News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Transparency and Early Planning Are Key in Increasing Efficiency of Gene Therapy Development for Rare Diseases
February 26, 2026 - NCATS News
- Platform Vector Gene Therapy (PaVe-GT)
PaVe-GT scientists underscore strategy, framework and early interaction with the FDA to align preclinical and clinical efforts in AAV gene therapy translation.
Read ArticleCures Within Reach Selected Three Clinical Trials in Rare/Ultra-Rare Diseases to Validate AI Predictions
February 25, 2026 - Grantee/Partner News
- Biomedical Data Translator (Translator)
NIH Awards Baylor More Than $15 Million to Fund Two Rare Diseases Consortia
September 30, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
NIH Awards $15M+ to Baylor-Led Consortia Targeting Rare Bone and Metabolic Disorders
September 27, 2025 - Media Coverage
- Rare Diseases Clinical Research Network (RDCRN)
NIH Awards More Than $15 Million to Fund Two Rare Diseases Consortia
September 25, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
NIH Awards $8.6 Million Grant to Renew Rare Disease Clinical Research Network for Neurodevelopmental Studies
September 15, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
Gene Editing Reverses Symptoms of Rare Brain Disorder in Mice
July 22, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
Genome Editing Corrected Rare Brain Mutations in Mice. Could It Help Fight Neurological Diseases?
July 21, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)