News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
NIH Awards $15M+ to Baylor-Led Consortia Targeting Rare Bone and Metabolic Disorders
September 27, 2025 - Media Coverage
- Rare Diseases Clinical Research Network (RDCRN)
NIH Awards More Than $15 Million to Fund Two Rare Diseases Consortia
September 25, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
Infant with Rare, Incurable Disease is First to Successfully Receive Personalized Gene Therapy Treatment
May 28, 2025 - NCATS News
- Our Impact on Rare Diseases
- Somatic Cell Genome Editing (SCGE)
NIH-supported gene-editing platform lays groundwork to rapidly develop treatments for other rare genetic diseases.
Repairing a Broken Code of Life: In CRISPR Breakthrough, Rewriting the Misspelling of Infant’s DNA Cures Him of Rare Liver Disease
May 16, 2025 - Grantee/Partner News
- Our Impact on Rare Diseases
- Somatic Cell Genome Editing (SCGE)
Personalized CRISPR Therapy Successfully Treats Infant With Rare, Incurable CPS1 Deficiency
May 16, 2025 - Media Coverage
- Our Impact on Rare Diseases
- Somatic Cell Genome Editing (SCGE)
Infant With Rare Incurable Disease Becomes First to Receive Successful Personalized Gene Therapy
May 15, 2025 - Media Coverage
- Our Impact on Rare Diseases
- Somatic Cell Genome Editing (SCGE)
Infant With Rare, Incurable Disease Is First to Successfully Receive Personalized Gene Therapy Treatment
May 15, 2025 - Grantee/Partner News
- Our Impact on Rare Diseases
- Somatic Cell Genome Editing (SCGE)
Researchers Identify Pathway Responsible for Calciphylaxis, a Rare and Serious Condition
April 23, 2025 - Grantee/Partner News
- Clinical and Translational Science Awards (CTSA) Program