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NCATS Collaboration Enables Gene Therapy to Move to Clinical Trial

NCATS and Duke University scientists help advance a gene therapy for Pompe disease into clinical testing for the first time.


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NCATS-Led Team Finds Potential Strategy to Fight Huntington’s Disease

A team of NCATS scientists and collaborators have uncovered a potential strategy against Huntington’s disease that may also be relevant to a range of neurodegenerative disorders.


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Rare Disease Day at NIH

This March 1, 2018 event features interactive panel discussions, posters, exhibits, tours and more. Register now.


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January E-Newsletter Now Available

Read about rare immune disorders research, CTSA Program training success stories, a new video about NCATS’ work to help patients with rare diseases, and more.


Consortium Charts New Course for Rare Immune Diseases

NCATS Rare Diseases Clinical Research Network scientists are conducting natural history studies and defining rare genetic diseases.


More Center News

Next Generation of Scientists

CTSA Program Fosters Next Generation of Translational Scholars.

Rare Diseases Research Video

Watch the new NCATS Rare Diseases Research Video, narrated by Dr. Petra Kaufmann.

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Director's Corner

Assay Guidance Manual

Assay Guidance Manual Cover

Interested in creating biologically, physiologically and pharmacologically relevant assays for early-stage drug discovery? Check out our best-practices Assay Guidance Manual.

Work with Us

Learn more about all the ways that potential grantees, partners and collaborators can access NCATS support to advance translational science.

  • NCATS Programs & Initiatives
    NCATS encourages partnerships that cross many scientific disciplines and research sectors in pursuit of translational success.
  • Small Business Opportunities
    NCATS’ small business programs help entrepreneurs develop and commercialize new translational technologies.
  • Expertise & Resources
    NCATS staff are experts in translation, and the Center’s resources support pre-clinical and clinical activities.
  • Licensing Opportunities
    NCATS makes it easy for industry and academia to interact and partner with Center laboratories and scientists.