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- Celebrating Wins Both Big and Small!
- Decreasing Cancer Disparities by Increasing Patient Understanding of Prognostic Genetics
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- About NCATS’ Role in the NIH HEAL Initiative
- Accelerating the Translation of Novel Compounds Toward INDs for Subsequent Clinical Testing
- Fiscal Year 2019 Funded Projects and Prizes
- NIH HEAL Initiative Funding & Collaboration Opportunities Led by NCATS
- Application Information for PAR-22-058: Emergency Awards: HEAL Initiative: Translational Science Career Enhancement Awards for Early and Mid-career Investigators (K18 Clinical Trials Not Allowed)
- Application Information for RFA-TR-22-012: Emergency Awards: HEAL Initiative-Limited Competition: HEAL Initiative Resource Centers for the Pain Management Effectiveness Research Network (ERN) (U24 Clinical Trial Not Allowed)
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- Announcement: Access to the COVID-19 Data Analytics Platform Now Open
- Media Advisory: To Improve Health on Earth, NIH-Funded Tissue Chips Push New Boundaries in Space
- NCATS Director Statement in Support of Ending Structural Racism and Health Disparities
- NCATS, Duke Scientists Show Compound’s Novel Effects on Key Brain Chemical in Drug Addiction
- NCATS, NRL Create Nanoparticle SARS-CoV-2 Model to Speed Drug Discovery for COVID-19
- NIH expands clinical trials to test convalescent plasma against COVID-19
- NIH launches analytics platform to harness nationwide COVID-19 patient data to speed treatments
- NIH, Tuskegee Researchers Develop Potential New Type of Immunotherapy Across Cancers and Many Other Diseases
- NIH-Supported Research Survey to Examine Impact of COVID-19 on Rare Diseases Community
- Rare Diseases Are Not Rare: Gallery of Creative Work Raises Awareness of Rare Diseases
- Releases & Announcements 2012
- Releases & Announcements 2013
- Releases & Announcements 2014
- CTSA Program Funding Opportunity Now Available
- NCATS Announces Funding Opportunities to Repurpose Drug Candidates from Industry
- NCATS Announces New Research Projects to Improve Treatments for Rare and Neglected Diseases
- NCATS Bridges Research Gaps in Developing Treatments for Diabetes-Related Blindness and Severe Heart Attacks
- NCATS Launches Chemical Toxicity Data Model Competition
- Petra Kaufmann Joins NCATS as Clinical Innovation Director
- Stephen Groft, Champion of Rare Diseases Research, Retires
- Releases & Announcements 2015
- Anton Simeonov Named NCATS Scientific Director
- Kaufmann Appointed Head of NCATS’ Office of Rare Diseases Research
- Lamirande to Lead NCATS Executive Office
- NCATS Announces CTSA Program Hub Awards to Help Transform How Clinical and Translational Science Is Conducted Nationwide
- NCATS Announces Tox21 Data Challenge Winners
- NCATS Director Statement on the Strategic Plan
- NCATS Seeks Applications to Repurpose Existing Drugs
- NCATS’ Preclinical Programs Now Accepting Collaborative Proposals
- New CTSA Program Funding Opportunities: Collaborative Innovation Awards
- New Funding Opportunities for Trial and Recruitment Innovation Centers
- Ramsey-Ewing Joins NCATS as OGMSR Director
- Researchers Working to Advance ExRNA Biomarkers and Therapies
- Releases & Announcements 2016
- NCATS Announces Funding Opportunity for New Bench-to-Clinic Repurposing Initiative
- NCATS Funds Feasibility Assessment to Develop Biomedical Data Translator
- NCATS to Fund Next Phase of Tissue Chip for Drug Screening Program
- NCATS to Support Tissue Chip for Drug Screening Testing Centers
- NCATS, CASIS Announce Funding Opportunity for Tissue Chip Research in Space
- Releases & Announcements 2017
- Releases & Announcements 2018
- NCATS Announces Joni Rutter as New Deputy Director
- NCATS Announces NIH HEAL-Related Funding Opportunities
- NCATS Funding Available to Repurpose Existing Drugs
- NCATS, Karolinska Institutet Scientists Attack Cancer’s Defenses
- NCATS-Led Team Finds Potential Strategy to Fight Huntington’s Disease
- NIH Awards $86 Million to Improve Genome Editing Techniques
- NIH Awards $86 Million to Improve Genome Editing Techniques
- NIH Hosts 2018 Rare Disease Day Event
- New Funding Opportunities Available for Collaborative Rare Diseases Research
- Tox21 Collaborators Release New Strategic Plan for Chemical Testing
- Releases & Announcements 2019
- A Promising Step in the Fight Against Lethal Childhood Brain Cancers
- NCATS Director Statement in Support of Diverse and Inclusive Meetings and Conferences
- NIH Awards $89 Million for Additional Projects to Advance Genome Editing
- NIH Funding Bolsters Rare Diseases Research Collaborations
- NIH funds new <i>All of Us</i> Research Program genome center to test advanced sequencing tools
- Rare Diseases Are Not Rare! Challenge Offers New Tools to Raise Awareness
- Tissue Chips in Space
- Releases & Announcements 2020
- Commonly Used Antibiotic Shows Promise for Combating Zika Infections
- NCATS Team’s Rapid Test Finds Promising Therapies for Myositis
- NCATS Translational Science Training Program Sets New Scientists on Paths to Career Success
- NIH Awards $35.5 Million to Use Tiny, Bioengineered Organ Models to Improve Clinical Trials’ Development and Design
- NIH Begins Large Clinical Trial to Test Immune Modulators for Treatment of COVID-19
- PaVe-GT: Collaborative NIH Effort Aimed at Creating a Gene Therapy Playbook, Making Rare Disease Treatments More Accessible
- Releases & Announcements 2021
- Assessing a Compound’s Activity, Not Just Its Structure, Could Deepen the Pool of Promising Drug Therapies
- Drug Testing Approach Uncovers Effective Combination for Treating Small Cell Lung Cancer
- Large Clinical Trial to Study Repurposed Drugs to Treat COVID-19 Symptoms
- NIH Study Suggests People with Rare Diseases Face Significantly Higher Health Care Costs
- NIH, FDA and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
- Scientists Identify Small-Molecule Cocktail to Improve Stem Cell Use in Research and Disease Treatments
- Releases & Announcements 2022
- Immune Modulator Drugs Improved Survival for People Hospitalized with COVID-19
- Media Advisory: To Find Answers for People on Earth, NIH-Funded Tissue Chip Models Take Flight
- Mount Sinai, NCATS Scientists Uncover a Potential New Path Against Neurological Disease
- Researchers Create 3-D Model for Rare Neuromuscular Disorders, Setting Stage for Clinical Trial
- Scientists Identify Characteristics to Better Define Long COVID
- Tiny Antibodies May Provide New Tool to Fight COVID-19
- Releases & Announcements 2023
- As Flights End, Tissue Chips in Space Projects Offer Glimpses Into the Biology of Aging
- NCATS Preclinical Therapeutic Development Programs Now Accepting Proposals to Collaborate
- NIH Gene Therapy Team Reveals Its Path to FDA Orphan Drug and Rare Pediatric Disease Designations
- New 3-D Model Offers Insights into the Role of Glucose in a Deadly Kidney Disease
- Researchers Show How a Tumor Cell’s Location and Environment Affect Its Identity
- Scientists Reveal a Potential New Approach to Treating Liver Cancer
- Statement on NIH Study Testing Convalescent Plasma in Hospitalized Patients
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- A New Method to Help Scientists Better Identify Drug Candidates
- Activating Key Cancer Enzyme Blocks Tumor Growth in Mice
- Tox21 Researchers Analyze Potential Negative Effects on Human Health of Thousands of Chemicals
- CTSA Program Community Mentorship Helps Advance Multiple Sclerosis Research in Latinos
- An Epigenetic Strategy to Kill Cancer Tumors
- Breathing Easier: First Treatment for Rare Lung Disease Approved
- Collaboration May Help Uncover Treatments for Rare Neurologic Disease
- Improved Disease Model Leads to Potential Therapy for Rare Disorder
- Lighting a Path for Improved Cancer Treatment
- Michael J. Fox Foundation Funds Research Project that Leverages NCATS Chemical Screening Approach and Resources
- Modeling the Female Reproductive Tract in 3-D: The Birth of EVATAR™
- NCATS Collaborative Project Wins Award for Excellence in Technology Transfer
- NCATS Plate Washing Initiative Saves Money, Keeps Plastic Out of Landfills
- NCATS Repurposing Test Identifies 53 Drugs that May Block Ebola Infection
- NCATS Research Team Identifies Possible Treatment for Niemann-Pick Type C1
- NCATS Researchers Propose Innovative Approach to Test Drugs in Rare Diseases
- NCATS Science Featured at 26th NIH Research Festival
- NCATS Science Featured at 28th NIH Research Festival
- NCATS Screening Technologies Enable Identification of Potential Treatment Target for Neurological Disorder
- NCATS Spotlight: Toxicology in the 21st Century (Tox21) Program
- NCATS Support Leads to Clinical Trial to Test Repurposed Cancer Treatment as Alzheimer’s Therapy
- NCATS Welcomes McInnes and Zuk to Leadership Team
- NCATS and Johns Hopkins Researchers Identify New Therapeutic Strategy for Eye Diseases
- NCATS’ Small Business Funding Helps Launch New Platform for Rare Diseases Drug Discovery
- NIH and Eli Lilly Publish Guide to Help Researchers Develop Therapeutic Screening Tests
- News Brief: Allergy Drug Could Treat Hepatitis C
- News Brief: Tox21 Researchers Publish Analysis of 10,000 Potentially Toxic Chemicals
- News Brief: Data Released on Drug Combinations to Treat Malaria
- News Brief: NCATS-FDA Team Receives HHS Innovation Ventures Support to Crowdsource Information on Treating Tropical Diseases
- Partnering with Disease Foundations to Speed Drug Discovery
- Screening Platform Is a Launch Pad for Novel Treatment Combinations
- Searching Saliva for Signs of Disease
- Spotlight on Collaboration: A Journey From Biological Probes to Potential Therapeutics
- Stopping Metastasis in Its Tracks: New 3-D Cell Model Enables Closer Look at Cancer Progression
- Study Demonstrates Success of NCATS’ Rare Diseases Therapeutic Development Programs
- TRND Research Leads to NIH Trial to Test Drug for Niemann-Pick Type C1
- 10,000 Compounds and Counting: Scientists Create Extensive Chemical Library to Study Toxic Substances, Share Data
- 2021 Rare Disease Day at NIH: Finding Hope Within Uncertainty
- 3-D Tissue Bioprinting: An Emerging Path to Better Drug Development
- An Itch to Scratch: NCATS, NIDCR Scientists Identify Potential New Approach to Chronic Problem
- Analysis Reveals Nationwide Spread of Three Historically Regional and Potentially Life-Threatening Fungal Infections
- Artificial Intelligence Is Advancing Clinical Research and Data Quality
- Automated Retinal Screening Opens a Window into People’s Health
- Better Method for Growing Stem Cells Could Speed Gene-Editing Therapies
- Brigham and Women’s Hospital and NCATS Scientists Dial Up an Approach Against Out-of-Control Inflammation
- Building Lung Tissue Models to Speed Virus Drug Testing
- COVID-19 Hospitalization May Increase Heart Failure Risk
- CTSA Program Researchers Aim to Improve Health Care from All Sides
- CTSA Program Support Enables Development of Life-Saving Blood Loss Monitor
- CTSA Program Support Kick-Starts Career and Emerging Research on Health Effects of Plastics
- CTSA Program-Supported Researchers May Turn Brown Fat into an Ally Against Obesity
- Can Metformin Treat COVID-19 and Prevent Long COVID? NCATS and Partners Pursue Answers
- Changing the Pill: Tackling Medication Adherence Through Innovative Technology
- Charting a New Path: NCATS Internship Helps Promising Student Soar
- Children Learn While They Play With Clinical-Trials Focused Coloring Book
- Clinical Trial Readiness Grants Aim to Set the Stage for Rare Disease Clinical Trials
- Closing the Protein Knowledge Gap to Identify New Treatments
- Collaborative Approach Aids Development of Potential Blood Test for Use in Alzheimer’s, Rare Syndromes Diagnoses
- Consortium in Action: Scientists Lay a Foundation for New Drug
- Drug Repurposing Approaches Reveal HIV Drug Holds Promise Against a Rare, Disabling Muscle Disorder
- Efficient Approach Creates Astrocytes Faster From Stem Cells for Drug Development and Regenerative Medicine
- Efficient Registry Approach Powers Practice-Shaping Infant Heart Surgery Trial
- Existing Drugs That Safeguard Endoplasmic Reticulum Could Point to Therapies for Many Diseases
- Finding What’s Common Among Diseases, Seeing the Bigger Picture
- Focusing on Cells Recycling Center, NCATS, Michigan Scientists Use High-Throughput Screening to Show Potential Approach Against Duchenne Muscular Dystrophy
- Genetic Analysis Suggests Dilated Cardiomyopathy Therapies May Work for Rare Peripartum Cardiomyopathy
- Genetics Experts Support Adding Hundreds of Treatable Rare Diseases to Newborn Screening
- Improving Manufacturing Techniques to Deliver High Quality Biotherapeutics to the Clinic Faster
- International Registry Reveals Risks COVID-19 Poses with Sickle Cell Disease
- Ketogenic Diet May Offer a New Approach to Treating Alzheimer’s Disease
- Low Vitamin D Levels May Boost COVID-19 Risk in Black People
- Lung Tissue Chips Could Help Predict Future Infectious Disease Variants
- N3C Data Reveal More Severe COVID-19 Outcomes in Rural Communities
- NCATS Assay Recognized in Top Ten List of Innovative Scientific Achievements
- NCATS BioPlanet: A Resource for Discovery
- NCATS Collaborations Lead to Potential New Drug Combinations for Childhood Cancers
- NCATS Creates Drug Development Data Portal
- NCATS Day Participants Share Perspectives to Advance Research Engagement
- NCATS Develops New Technique to Look Inside Cells Growing in 3-D
- NCATS Explores Science with Middle School Students
- NCATS Funds Network to Improve the Use of Telehealth in Children’s Health Care
- NCATS Funds New Drug Repurposing Projects, Seeks Additional Industry Partners
- NCATS Ignites Translational Science Spark for Young Investigators
- NCATS Innovation Continues Through Latest HHS Ignite Team Selections
- NCATS Makes Science Fun for Local Middle Schoolers
- NCATS Patent Book Showcases Opportunities for Collaborations and Licensing
- NCATS Releases Updated Translational Road Maps
- NCATS Researchers Develop New Approach to Identify Potential Cancer Drugs
- NCATS Researchers’ New Approach to Measure Gene Activity Could Speed Search for Rare Disease Therapies
- NCATS Scientists Prioritize Compounds to Advance Research on Mitochondrial Damage
- NCATS Scientists Turn Stem Cells Into Vast Supply of Neurons to Better Predict Pain Therapies’ Effectiveness
- NCATS Spearheads a New Resource for Natural Products
- NCATS Supports Award-Winning Technology for Drug Development
- NCATS Unveils Patient-Focused Therapy Development Toolkit
- NCATS, FDA Co-Host Workshop on Gene Therapy for Rare Diseases
- NCATS-Supported Consortium Charts New Course for Rare Immune Diseases
- NCATS-Supported Research Reduces Time to Diagnosis for Seriously Ill Children with Genetic Diseases
- NCATS-Supported Researchers Find Cell Source Matters for Tissue Chips
- NCATS-Supported Researchers Find Exercise May Help Protect DNA
- NCATS’ Preclinical Collaboration Enables Gene Therapy for Rare Muscle Disease to Advance to Clinical Trial
- NCATS’ Screening Studies Focus on Making Melanoma Cells More Visible, Advancing Efforts to Overcome Roadblock in Therapy
- NIH-Supported Research Helps Advance a Potential Rare Disease Gene Editing Treatment into Clinical Trials
- NIH-Supported Researchers Use Robots, Stem Cells to Produce Organ Models
- NIH-Supported Scientists Discover New Personalized Approach to Diagnosing and Treating Rare Food Allergy Disease
- NIH-Supported Scientists Uncover Clues to Spinal Cord Development, Neurodegenerative Disease
- National EHR Data Resource Reveals COVID-19’s Stark Mortality Risk in People with COPD
- Nationwide IRB Reliance Agreement Aimed at Speeding Research Reaches 1,000 Signatories
- New 3-D Models Offer Insights Into the Biology of a Rare, Devastating Neurological Disease
- New Method Could Help Find Potential Treatments for Rare Diseases
- New NCATS-Supported Test Could Provide Faster Diagnosis of Deadly Disease
- Opioids Increase the Risk of Pneumonia
- Patient Perspectives and Hope of Research Defined 10th Annual Rare Disease Day at NIH
- Previous Common Colds Could Boost Risks of More Severe COVID-19
- Rare Disease Day at NIH 2022: Shining a Light on Patient Perspectives
- Rare Disease Day at NIH 2023: Putting Hope Into Action
- Rare Disease Day at NIH: Drawing Hope and Building Connections Across the Community
- Rare Disease Patients and Families Find Hope in Research
- Reflecting on a Remarkable 2019
- Repurposed Drug Approach May Thwart Spread of Cancer Cells
- Researchers Convene to Take Stock and Take Action in the Opioid Crisis
- Researchers Use Cutting-Edge EHR Data Resource to Find Risk Factors for Severe COVID-19 in Children
- Robots Could Spur Use of Stem Cells in the Laboratory and Clinic
- Rural Hospital Closures Fuel Rising Demand and Costs at Nearby Hospitals
- Small Business Awards Propel the Development of a “One-of-a-Kind” Tissue Chip Technology
- Study Finds Immune Dysfunction Is a Significant Risk Factor for COVID-19 Breakthrough Infection
- Target Watch Sheds Light on Overlooked Proteins
- Templates for Success: Speeding the Formation of Public-Private Partnerships
- The Beat Goes On — Even 258 Miles Above Earth
- Tissue Chip Projects Highlighted in Major Journal
- Tissue Chip Researchers Create a Working Model of a Heart Chamber
- Tissue Chip Trio to Orbit Earth for Answers to Osteoarthritis and Muscle Diseases
- Tissue Model Approach Provides Clues to SARS-CoV-2 Brain Infections
- Translator: Unique Collaborative Approach to Advancing Biomedical Data Sharing
- Unexpectedly Following a Translational Science Path
- Working Together Is the Name of the Game at Rare Disease Day at NIH
- Tox21 Collaboration Generates an Innovative Platform for Testing Individual Differences in Chemical Sensitivity
- Doctoral Students Use NCATS Resources to Investigate Promising Disease Therapies
- NCATS Furthers Efforts to Create a Data Ecosystem to Explore Disease Connections
- NCATS Small Business Award Seeds App to Improve Medication Adherence
- NIH I-Corps Training Helps NCATS-Supported Companies Find Their Way
- NIH, Academia and Patient Advocate Collaboration Speeds Niemann-Pick Type C1 Research
- News Brief: NCATS Announces Quarterly Update to Its Assay Guidance Manual
- News Brief: NCATS SMART IRB Team Launches Online Reliance System
- News Brief: NCATS Scientists Participate in NIH Research Festival
- News Brief: NCATS Staff to Test Innovative Ideas for HHS
- News Brief: NYU CTSA Program Hub Hosts Science Café
- News Brief: NYU CTSA Program Hub Releases Research Study Recruitment E-Book
- Small Business Award Spurs Innovation to Improve Data Use
- Understanding the Brain’s Response to Sugar Could Help Treat Obesity
- First NCATS Day Demonstrates Commitment to Patients Through Smarter Science
- NCATS E-Newsletter
- Past E-Newsletter Issues
- Collaborate with NCATS Scientists
- FDA-NIH BEST Biomarker Glossary Now Available
- NCATS Closes Small Molecule Repository
- NCATS Hosts Assay Guidance Workshop
- NCATS Hosts Early Career NIH Scientists for Translational Science Training Program
- NCATS Seeks New Drug Development Partners and Pharmaceutical Assets
- NCATS Stem Cell Translation Laboratory Grand Opening
- NCATS and FDA Host Assay Guidance Workshop for High-Throughput Screening and Lead Discovery
- NCATS and Promega Host Assay Guidance Workshop for High-Throughput Screening
- New Chapters Added to the Assay Guidance Manual
- New Chapters, Updates to the Assay Guidance Manual
- Pfizer’s Centers for Therapeutic Innovation Proposal Portal Opens September 6
- Translational Science Representatives Meet to Advance Field
- Past E-Newsletter Issues
- I Am Translational Science
- Scientific Publications
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- About NCATS
- Center Overview
- About the Center
- Director’s Corner
- 2012 Director’s Messages
- 2013 Director’s Messages
- 2014 Director's Messages
- 2015 Director’s Messages
- 2016 Director’s Messages
- 2017 Director’s Messages
- 2018 Director’s Messages
- April 11, 2022: A Decade to Deliver Five Times More Treatments
- April 15, 2021: The work of translational science has just begun
- April 19, 2023: NCATS’ New Strategic Plan Will Chart a Path for Realizing Our Audacious Goals
- April 30, 2020: Inspiring Progress on All Fronts in the Translational Science Fight Against COVID-19
- April 9, 2019: Applying Translational Science to Address Rural Health Disparities
- August 15, 2019: Developing Principles of Patient Engagement with The Children’s Inn at NIH
- August 17, 2022: New Treatments Twice as Fast
- August 31, 2020: A different kind of COVID-19 (sero)survey
- Dec. 1: 2020: ACTIVating translational science to treat COVID-19
- Dec. 21, 2020: In response to unprecedented challenges, a breakthrough year for translational science
- December 18, 2019: Reflecting on NCATS’ 2019 Activities
- Director’s Biography
- Feb. 5, 2019: Rare Diseases Are Not Rare!
- February 17, 2022: Rare Diseases Have a Home at NCATS
- February 26, 2021: Informatics: The ultimate translational team sport
- February 27, 2020: Resource for Systemizing Serendipity Turns 10
- February 6, 2023: Five Lessons NCATS Learned During the Pandemic
- Jan. 2, 2019: Blast Off to New Translational Science Horizons
- Jan. 26, 2017: Applying Effective Translational Team Models Across NCATS
- January 19, 2022: The Decade Ahead: More Treatments for All People More Quickly
- January 27, 2020: The Personal and Public Health Imperative of Rare Diseases
- January 28, 2021: Bringing urgency to the public health issue of rare diseases
- July 10, 2018: Bringing Translational Science to the Opioid Crisis
- July 17, 2019: Reflecting on Our Own “Space” Explorations on the 50th Anniversary of the Apollo 11 Moon Landing
- July 30, 2021: NCATS Is Preparing for Tomorrow’s Pandemics Today
- July 31, 2020: Translation for all
- June 13, 2019: Establishing Education and Training for the Young Field of Translational Science
- June 27, 2023: How NCATS Tackles Persistent Problems in Translation
- June 3, 2021: NCATS and Translational Science: Contributing to a Post-COVID-19 Pandemic World
- June 30, 2020: Manifesting and empowering data sharing for COVID-19 and beyond
- June 8, 2022: Increase Inclusivity to Improve Health for All
- Leading NCATS into the Future
- March 11, 2019: Applying “Translational Rigor” to Address the Opioid Crisis
- March 18, 2021: Dr. Christopher P. Austin to step down as NCATS director
- March 31, 2020: Practicing Physical Distancing and Bringing Our Science to Combat COVID-19
- May 16, 2019: Examining Precision Medicine Through a Rare Diseases Lens
- May 29, 2020: Creating the data platforms needed to guide our response to COVID-19
- November 26, 2019: NCATS Day 2019: Conversations on Responsible Data Sharing
- November 4, 2021: Accelerating Health Solutions for All: Reflections on NCATS and ARPA-H
- Oct. 29, 2020: NCATS’ commitment to community engagement contributes to reducing COVID-19 health disparities
- October 31, 2019: Full Speed Ahead: Bringing Translational Science to the Opioid Crisis
- October 5, 2021: Dr. Collins’ Impact on NIH, NCATS and Beyond
- September 15, 2022: Engaging “Many Hands” to Advance NCATS’ Mission
- September 26, 2019: We Want Your Input on the CTSA Program to Ensure Our Collective Success!
- NCATS Strategic Plan
- NCATS Staff Profiles
- Staff Profile: Alexey V. Zakharov
- Staff Profile: Adam Yasgar
- Staff Profile: Alice Chen
- Staff Profile: Amanda L. Vogel
- Staff Profile: Ami D. Gadhia
- Staff Profile: Andre Pilon
- Staff Profile: Andrew Kelly
- Staff Profile: Andrés Dulcey
- Staff Profile: Angie Cruz-Albertorio
- Staff Profile: Ann R. Knebel
- Staff Profile: Anna J. Rossoshek
- Staff Profile: Anton Simeonov
- Staff Profile: Atena Farkhondeh Kalat
- Staff Profile: Bekah E. Geiger
- Staff Profile: Bobbi Gardner
- Staff Profile: Carlos A. Tristan
- Staff Profile: Christine Colvis
- Staff Profile: Christine M. Cutillo
- Staff Profile: Christopher J. Dillon
- Staff Profile: Christopher S. Maurer
- Staff Profile: Claire Malley
- Staff Profile: Clare K. Schmitt
- Staff Profile: Craig Thomas
- Staff Profile: Dammika Amugoda
- Staff Profile: Daniel C. Talley
- Staff Profile: Danilo Tagle
- Staff Profile: David Gerhold
- Staff Profile: David W. Kim
- Staff Profile: David Wilde
- Staff Profile: Dobrila D. Rudnicki
- Staff Profile: Dorjbal Dorjsuren
- Staff Profile: Elaine Collier
- Staff Profile: Elizabeth A. Ottinger
- Staff Profile: Emily Carlson Marti
- Staff Profile: Enrique S. Lagos
- Staff Profile: Eric Wk Sid
- Staff Profile: Erica Rosemond
- Staff Profile: Abir N. Malik
- Staff Profile: Ainslie Tisdale
- Staff Profile: Alex J. Vendola
- Staff Profile: Alumit Ishai
- Staff Profile: Andie Vaught
- Staff Profile: Andrew N. Louden
- Staff Profile: Angela A. Steadman
- Staff Profile: Angelica Medina
- Staff Profile: Anna L. Ramsey-Ewing
- Staff Profile: Anu Dalal
- Staff Profile: Ashli N. Holloway
- Staff Profile: Audie A. Atienza
- Staff Profile: Belen Hurle
- Staff Profile: Brittany M. Gibbons
- Staff Profile: Cara L. Purdy
- Staff Profile: Chariz P. Johnstone
- Staff Profile: Christine M. Happel
- Staff Profile: Christopher M. Hartshorn
- Staff Profile: Dirgha Raj Joshi
- Staff Profile: Djawed Bennouna
- Staff Profile: Dmitriy V. Krepkiy
- Staff Profile: Edward Wu
- Staff Profile: Elena M. Hausmann
- Staff Profile: Elizabeth E. Conklin
- Staff Profile: Emily J. Davis
- Staff Profile: Emily M. Lee
- Staff Profile: Eric J. Juarez
- Staff Profile: Ericka Y. Shipp
- Staff Profile: Erin A. Davis
- Staff Profile: Geetha Senthil
- Staff Profile: Gloria F. Velez
- Staff Profile: Gregory P. Jarosik
- Staff Profile: Guadalupe (Lupe) V. Aquino
- Staff Profile: Gyutae Lim
- Staff Profile: Haksong Jin
- Staff Profile: Haley A. Chatelaine
- Staff Profile: Harrison C. Daly
- Staff Profile: Heather L. Baker
- Staff Profile: Hoda Zarkoob
- Staff Profile: Imoni M. Williams
- Staff Profile: Jaleal S. Sanjak
- Staff Profile: James J. Taylor
- Staff Profile: Jasmine Kalsi
- Staff Profile: Jeannette L. Johnson
- Staff Profile: Jennie L. Conroy
- Staff Profile: Jennifer J. Cho
- Staff Profile: Jennifer M. Beierlein
- Staff Profile: Jessica C. Walrath
- Staff Profile: Jessica M. Freilino
- Staff Profile: Jing Chen
- Staff Profile: Joanne M. Lumsden
- Staff Profile: Jori Contee Staten
- Staff Profile: Jose F. Ruiz
- Staff Profile: Josh Fessel
- Staff Profile: Katie L. Matthews
- Staff Profile: Kelli M. Wilson
- Staff Profile: Ken L. Wiley, Jr.
- Staff Profile: Kihwa Kang
- Staff Profile: Krisann Freilino
- Staff Profile: Kun Shen
- Staff Profile: Laura (Hope) Shapiro
- Staff Profile: Laura L. Bailey Joell
- Staff Profile: Leah Tolosa Croucher
- Staff Profile: Leslie Le
- Staff Profile: Linda D. Ho
- Staff Profile: Louis V. Choporis
- Staff Profile: Marissa E. Davies
- Staff Profile: Meena U. Rajagopal
- Staff Profile: Megan E. Cowles
- Staff Profile: Megan P. Jackson
- Staff Profile: Miao Xu
- Staff Profile: Michael H. Forde
- Staff Profile: Michael H. Ronzetti
- Staff Profile: Molly Congdon
- Staff Profile: Monika Rajput
- Staff Profile: Munziba T. Khan
- Staff Profile: Naomi R. Freeman
- Staff Profile: Neena A. Gohil
- Staff Profile: Nicole J. Garbarini
- Staff Profile: Patrick H. Brown
- Staff Profile: Patrick J. Morris
- Staff Profile: Qi Zhang
- Staff Profile: Qian Zhu
- Staff Profile: Quinlin M. Hanson
- Staff Profile: Rachel R. Ratz
- Staff Profile: Rebecca A. Erwin-Cohen
- Staff Profile: Rintaro Kato
- Staff Profile: Rodica Stan
- Staff Profile: Salina P. Waddy
- Staff Profile: Sanae ElShourbagy Ferreira
- Staff Profile: Sarah E. Dunsmore
- Staff Profile: Sean R. Gardner
- Staff Profile: Seungmi Ryu
- Staff Profile: Shannon Oden
- Staff Profile: Shuaizhang Li
- Staff Profile: Stacey A. Fakinlede
- Staff Profile: Stephanie B. Mounaud
- Staff Profile: Stephanie H. Ezequiel
- Staff Profile: Steve Elsberg
- Staff Profile: Stuart G. Kern
- Staff Profile: Tara D. Eicher
- Staff Profile: Tej Poudel
- Staff Profile: Thomas C. Radman
- Staff Profile: Tiangay F. Waines
- Staff Profile: Tim Page
- Staff Profile: Tino W. Sanchez
- Staff Profile: Venkata R. Mangalampalli
- Staff Profile: Victor M. Henriquez
- Staff Profile: Wenyu Zeng
- Staff Profile: Yanji Xu
- Staff Profile: Yolanda F. Vallejo
- Staff Profile: Yong-Mo Ahn
- Staff Profile: Yu-Chih Lin
- Staff Profile: Zulema Eldridge
- Staff Profile: Eugen Buehler
- Staff Profile: Ewy A. Mathé
- Staff Profile: G. Sitta Sittampalam
- Staff Profile: Gallya Gannot
- Staff Profile: Ganesha Rai
- Staff Profile: Gergely Zahoránszky-Kőhalmi
- Staff Profile: Gregory J. Tawa
- Staff Profile: Hongmao Sun
- Staff Profile: Hu Zhu
- Staff Profile: James E. Dickens
- Staff Profile: James Inglese
- Staff Profile: Jamie Mihoko Doyle
- Staff Profile: Jane C. Atkinson
- Staff Profile: Jason Rohde
- Staff Profile: Jennifer L. Kouznetsova
- Staff Profile: Joan Davis Nagel
- Staff Profile: Joni L. Rutter
- Staff Profile: Juan Marugan
- Staff Profile: Julianna E. Romaniuk
- Staff Profile: Karlie R. Sharma
- Staff Profile: Keith R. Lamirande
- Staff Profile: Kenneth R. Gersing
- Staff Profile: Krishna “Balki” Balakrishnan
- Staff Profile: LaKeshia Wood
- Staff Profile: Li Liu
- Staff Profile: Madhu Lal-Nag
- Staff Profile: Mahesh Aitha
- Staff Profile: Mahtab Moghiminia
- Staff Profile: Marc Ferrer
- Staff Profile: Marcus G. Hodges
- Staff Profile: Mark J. Henderson
- Staff Profile: MarySheyla K. Alvarez
- Staff Profile: Matthew D. Hall
- Staff Profile: Matthew T. Zeback
- Staff Profile: Mayra A. Alvarez Lopez
- Staff Profile: Meera A. Shah
- Staff Profile: Menghang Xia
- Staff Profile: Meredith D. Temple-O’Connor
- Staff Profile: Michael G. Kurilla
- Staff Profile: Min Shen
- Staff Profile: Monica L. Carter-Donerson
- Staff Profile: Natalia Martinez
- Staff Profile: Nathan Coussens
- Staff Profile: Nichol M. Cleveland
- Staff Profile: Pablo Cure
- Staff Profile: Passley R. Hargrove-Grimes
- Staff Profile: Patricia K. Dranchak
- Staff Profile: Peggy McClelland
- Staff Profile: Penny Burgoon
- Staff Profile: Philip E. Sanderson
- Staff Profile: Philip John (P.J.) Brooks
- Staff Profile: Prachi K. Patel
- Staff Profile: Pramod S. Terse
- Staff Profile: Rajarshi Guha
- Staff Profile: Rashmi Gopal-Srivastava
- Staff Profile: Raul Calvo
- Staff Profile: Rebecca Katz
- Staff Profile: Rhishikesh R. Bargaje
- Staff Profile: Richa M. Lomash
- Staff Profile: Robert J. Schneider, Jr.
- Staff Profile: Ruili Huang
- Staff Profile: Ryan MacArthur
- Staff Profile: Sabine C. Alexander
- Staff Profile: Samarjit Patnaik
- Staff Profile: Sandeep Rana
- Staff Profile: Sankalp Jain
- Staff Profile: Sean J. Finnegan
- Staff Profile: Senetra L. Brown
- Staff Profile: Sharie J. Haugabook
- Staff Profile: Shyh-Ming Yang
- Staff Profile: Soju Chang
- Staff Profile: Stacia H. Fleisher
- Staff Profile: Stephanie L. Ford-Scheimer
- Staff Profile: Stephen G. Seidel
- Staff Profile: Stephen Kales
- Staff Profile: Steven I. Benowitz
- Staff Profile: Steven T. Pittenger
- Staff Profile: Surendra Karavadhi
- Staff Profile: Sury Vepa
- Staff Profile: Tao Deng
- Staff Profile: Terrence E. Rudd, Jr.
- Staff Profile: Tierra E. Clarke
- Staff Profile: Tiina K. Urv
- Staff Profile: Timothy Sheils
- Staff Profile: Tyler F. Beck
- Staff Profile: Vukasin Jovanovic
- Staff Profile: Wei Sun
- Staff Profile: Wei Zheng
- Staff Profile: Wenjuan Ye
- Staff Profile: Wenwei Huang
- Staff Profile: William F. Borschel
- Staff Profile: Xin Hu
- Staff Profile: Xin Xu
- Staff Profile: Yuhong Wang
- Staff Profile: Zoe-Ann I. Copeland
- NCATS Programs & Initiatives
- 3-D Tissue Bioprinting Program
- Stem Cell Translation Laboratory
- Assay Development and Screening Technology (ADST)
- Biomedical Data Translator
- Bridging Interventional Development Gaps (BrIDGs)
- About BrIDGs
- BrIDGs Scientific Capabilities
- Work with BrIDGs
- BrIDGs Projects
- Active BrIDGs Projects
- BPN14770 for Treatment of Fragile X Syndrome
- Development of Drinabant for Treatment of Acute Cannabinoid Overdose
- Development of Nogo Receptor Decoy for the Treatment of Spinal Cord Injury
- Evaluation of ACT1 to Treat Diabetic Keratopathy
- IND-Enabling Preclinical Studies of 2DG for Treatment of Epilepsy
- Manufacture of RLIP76-LyoPL for Acute Radiation Syndrome
- Peripheral CB1 Receptor Antagonist for Therapeutic Use in Metabolic Syndrome
- Preclinical Development of EDN-OL1 for Alzheimer’s Disease
- Short Stabilized EPO-Peptide as Therapeutic Agents for Multiple Sclerosis and Acute Brain Trauma
- Studies of Tumor-Penetrating Microparticles for Pancreatic Cancer
- Targeted Bone Regeneration via Activation of Resident Stem Cells
- Toxicity Studies of Nebulized Propofol Hemisuccinate
- Completed BrIDGs Projects
- A Novel Drug Candidate for the Treatment of Diabetic Retinopathy
- A Potent Oral Therapy for Cytomegalovirus Infection
- Advanced Studies with 5HMF—Most Potent Anti-Sickling Agent
- Alternative Formulations of Decitabine to Reactivate Fetal Hemoglobin Production
- Biomimetic Actinide Decorporation Agents: Enabling Availability
- Developing SRX246 for Stress-Related Affective Illness
- Development of Assays to Detect Anti-Drug Antibodies Against ACP-501
- Development of Bone Morphogenetic Protein Inhibitors to Treat Blood and Bone Disorders
- Development of Exendin-(9-39) for the Treatment of Congenital Hyperinsulinism
- Development of HGF Mimetic (Refanalin) for Hepatic Fibrosis
- Development of Minihepcidins for the Treatment of Beta Thalassemia
- Development of Neurosteroids for Lysosomal Storage Disorders
- Development of P-321 for Chronic Dry Eye
- Development of an ApoA-1 Mimetic Peptide for Treatment of Atherosclerosis
- Enabling Toxicology Safety Pharmacology Studies for First-in-Class CPG-Activating Drug Treatment Against Chronic Spinal Injury
- HBN-1 Regulated Hypothermia Formulation and Evaluation of Toxicity
- IND-Enabling Studies on AAV2-GDNF for Parkinson’s Disease
- IND-Enabling Toxicology and Safety Pharmacology Studies of ATN-161 for the Treatment of Crohn’s Disease
- Inhibitors of Glutaminase 2 as Therapeutic Agents for Neuro-Oncological Diseases and Celiac Sprue
- Large-Scale Synthesis of Clozapine-N-Oxide
- Long-Acting Parathyroid Hormone Analog for Treatment of Hypoparathyroidism
- Manufacture of AAV2-AADC for the Treatment of AADC Deficiency
- Metarrestin for the Treatment of Pancreatic Cancer
- Metastin Administration in Humans: Support for Preclinical Toxicology Studies
- Novel PDE Inhibitors for Treatment of Cognitive Dysfunction in Schizophrenia
- Novel Pre-Hospital Therapy of Myocardial Infarction
- Pharmacological and Toxicological Evaluation of the Gene Transfer Vectors for osteoarthritis
- Preclinical Development of CDD-0102 for the Treatment of Alzheimer’s Disease
- Redox Encrypted Therapeutics for Treatment of Friedreich’s Ataxia
- Safety Pharmacology Studies for Beta Thalassemia
- Single-Chain Urokinase Plasminogen-Activating Factor
- Small Molecule Treatment for Rheumatoid Arthritis
- Using the Preimplantation Factor (PIF) to Treat Graft-Versus-Host Disease
- cGMP Synthesis of the Selective Kappa Opioid Receptor Antagonist JDTic
- Active BrIDGs Projects
- Chemistry Technology
- About Chemistry Technology
- Chemistry Technology Scientific Capabilities
- Work with Chemistry Technology
- Chemistry Technology Projects
- Active Chemistry Technology Projects
- Development of (2R,6R)-Hydroxynorketamine
- Development of Dual-Acting IRAK/FLT3 Inhibitors for Acute Myeloid Leukemia (AML) and Myelodysplastic Syndromes (MDS)
- Development of a Novel Inhibitor of Fumarate
- Development of a Small Molecule Inhibitor
- Development of an Activator of the Pyruvate Kinase Isoform M2 (PKM2)
- Development of the αllbß3 Antagonist RUC-4 for the Treatment
- Completed Chemistry Technology Projects
- A BODIPY Conjugate of the BCR-ABL Kinase Inhibitor Nilotinib
- A Role for RDEA-119 Within the Treatment of Marfan Syndrome
- A Role for Tofacitinib With the Treatment of Adult T Cell Leukemia & HTLV-I-Associated Myelopathy/Tropical Spastic Paraparesis
- BMS-509744 as Chemical Probe for Studying the Role of Inducible T Cell Kinase in HIV Replication
- Incorporating Stable Glycosides into Novel Small Molecule Scaffolds
- Inhibitors of NAD-Dependent 15-Hydroxyprostaglandin Dehydrogenase for the Study of Prostaglandin's Role in Inflammation
- Small Molecule Combinations for Basic and Translational Studies
- Active Chemistry Technology Projects
- Discovering New Therapeutic Uses for Existing Molecules
- Genetic and Rare Diseases Information Center (GARD)
- Matrix Combination Screening
- About Matrix Combination Screening
- Matrix Screening Scientific Capabilities
- Work with Matrix Screening
- Matrix Screening Projects
- Development of Novel Chemical Genomic Platforms for Pathogenic Protozoa
- High-Throughput Combinatorial Screening Identifies Drugs that Cooperate with Ibrutinib to Kill Activated B-Cell-Like Diffuse Large B-Cell Lymphoma Cells
- High-Throughput Drug Screening Identifies Novel Therapeutic Options for BPDCN
- Identification of a Synergistic Combination Between PARP Inhibitors and NAMPT Inhibitors in Ewing Sarcoma
- PAX3-FOXO1 Establishes Myogenic Super Enhancers and Confers BET Bromodomain Vulnerability
- mQC: A Quality Control Metric for High-Throughput Combination Screening
- Early Translation Branch (ETB)
- A Specialized Platform for Innovative Research Exploration (ASPIRE)
- A Translational Approach to Addressing COVID-19
- Antiviral Program for Pandemics
- Clinical Trial Readiness for Rare Diseases, Disorders and Syndromes
- Multidisciplinary Machine-Assisted, Genomic Analysis and Clinical Approaches to Shortening the Rare Diseases Diagnostic Odyssey
- National COVID Cohort Collaborative (N3C)
- The Accelerating Medicines Partnership® Bespoke Gene Therapy Consortium (BGTC)
- NIH Common Fund Programs
- Rare Diseases Registry Program (RaDaR)
- Tissue Chip for Drug Screening
- About Tissue Chip
- Tissue Chip Funding Information
- Tissue Chip Initiatives & Projects
- Meet Chip
- Toxicology in the 21st Century (Tox21)
- Functional Genomics Lab
- Therapeutics for Rare and Neglected Diseases (TRND)
- About TRND
- TRND Scientific Capabilities
- Work with TRND
- TRND Projects
- Active TRND Projects
- Completed TRND Projects
- A Protein Replacement Drug for Friedreich’s Ataxia
- AVI-4038 for Treatment of Duchenne Muscular Dystrophy
- Aes-103 for Sickle Cell Disease
- Antifibrotic Therapy for the Treatment of Pulmonary Hypertension
- Auranofin for Chronic Lymphocytic Leukemia
- Bone Morphogenetic Protein Inhibitors to Treat Fibrodysplasia Ossificans Progressiva
- CMX001 for Treatment of Neonatal Herpes Simplex Virus
- Cyclodextrin for Niemann-Pick Type C1 Disease
- DEX-M74 for GNE Myopathy (Hereditary Inclusion Body Myopathy)
- Deuterated Analogs of Praziquantel for Treatment of Schistosomiasis
- Development of Acoziborole for the Treatment of Human African Trypanosomiasis
- Development of Oxadiazoles as Treatment for Schistosomiasis and Hookworm
- Development of VBP15 for Treatment of Duchenne Muscular Dystrophy
- Development of a Therapeutic for Lassa Fever
- Development of the Novel Antifungal VT-1129 for Cryptococcal Meningitis
- Gene Therapy for the Treatment of AADC Deficiency
- Gene Therapy for the Treatment of Pompe Disease
- Inhaled GM-CSF Therapy for Autoimmune Pulmonary Alveolar Proteinosis
- LUM-001 as a Treatment for Creatine Transporter Deficiency
- Novel Treatment for Hermansky-Pudlak Syndrome Pulmonary Fibrosis
- PAK Inhibitor for Fragile X Syndrome
- Repurposing an EU Therapeutic for Hemoglobinopathies
- Small Molecule Pharmacological Chaperone for the Treatment of Autosomal Dominant Retinitis Pigmentosa
- Therapy for Fuchs Endothelial Corneal Dystrophy
- Treatment of Acid Ceramidase Deficiency
- Use of Rapamycin for the Treatment of Hypertrophic Cardiomyopathy in Patients with Noonan Syndrome with Multiple Lentigines (NSML)
- Use of Retinal Progenitor Cells for the Treatment of Retinitis Pigmentosa
- TRND Clinical Research Studies
- Drug Repurposing Screening for Rare and Neglected Diseases
- Gene Therapy Platform for Rare Diseases
- Work with NCATS
- Advisory Groups
- NCATS Advisory Council
- Council Roster
- Council Meetings
- January 2015 Council/CAN Review Board Meeting
- January 2016 Council/CAN Review Board Meeting
- January 2017 Council/CAN Review Board Meeting
- June 2015 Council/CAN Review Board Meeting
- June 2016 Council/CAN Review Board Meeting
- May 2017 Council/CAN Review Board Meeting
- September 2015 Council/CAN Review Board Meeting
- September 2016 Council/CAN Review Board Meeting
- Council Subcommittees and Working Groups
- General Council Operating Procedures
- Council Concept Clearances
- NCATS Advisory Council
- Center Overview
- News & Media
- Funding & Notices
-