News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
How Repurposing a Drug May Help Treat More Rare Gastrointestinal Diseases
June 29, 2026 - NCATS News
- Rare Diseases Clinical Research Network (RDCRN)
RDCRN researchers found that dupilumab — a drug used for asthma and chronic obstructive pulmonary disease — shows promise in treating eosinophilic gastritis.
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FDA Clears IND for Gene Therapy Candidate to Treat Rare Metabolic Disorder
May 21, 2026 - NCATS News
- Our Impact on Clinical Trials
- Our Impact on Drug Discovery and Development
- Our Impact on Rare Diseases
MMA-101, an NIH-supported AAV gene therapy for a rare metabolic disorder, has received FDA clearance to begin clinical testing.
Read ArticleLooking for the Common in Rare
July 20, 2024 - Grantee/Partner News
- Our Impact on Rare Diseases
Using AI to Improve Detection of Rare Diseases
July 16, 2024 - Grantee/Partner News
- Clinical and Translational Science Awards (CTSA) Program
Paving the Way for Ultrarare Bone Disease Treatment Trial
May 21, 2024 - NCATS News
- Our Impact on Drug Discovery and Development
- Therapeutics for Rare and Neglected Diseases (TRND)
Clinicians at the NIH Clinical Center will soon start testing an investigative drug for an ultrarare bone disease. Efforts from NCATS’ scientists helped make this research milestone possible.
EveryLife Foundation Announces Scientific Workshop on ‘Ultra-Rare’ Diseases
May 16, 2024 - Media Coverage
- Our Impact on Rare Diseases
Every Cure Gets $48 Million for AI-Powered Rare Disease Research
May 14, 2024 - Grantee/Partner News
- Clinical and Translational Science Awards (CTSA) Program
Rare Disease Day at NIH 2024: Showcasing Voices and New Opportunities
April 23, 2024 - NCATS News
- Our Impact on Rare Diseases
The rare diseases community came together at Rare Disease Day at NIH to share inspiring stories, impactful research advances and exciting new possibilities for the future.