News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
A Rare Respiratory Disease May Be More Prevalent in Quebec
November 27, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
NIH Awards Baylor More Than $15 Million to Fund Two Rare Diseases Consortia
September 30, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
Global Patient Registries Can Advance Opportunities for Rare Disease Research
December 14, 2023 - Media Coverage
- Rare Diseases Registry Program (RaDaR)
Rare Syndrome After COVID Vaccines Described
December 1, 2023 - Media Coverage
- Clinical and Translational Science Awards (CTSA) Program
Newborn Screening for Rare Immune Disorders Led to Earlier Treatment, Improved Survival
November 20, 2023 - NCATS News
- Rare Diseases Clinical Research Network (RDCRN)
An NCATS-led Rare Diseases Clinical Research Network consortium changed what is known about severe combined immunodeficiency. Researchers developed lifesaving therapies for the disease and pioneered a screening test for newborns.
Pushing for Better Clinical Trial Design for Rare Diseases
October 17, 2023 - Grantee/Partner News
New 3-D Models Offer Insights Into the Biology of a Rare, Devastating Neurological Disease
July 28, 2023 - NCATS News
- 3-D Tissue Bioprinting
- Therapeutics for Rare and Neglected Diseases (TRND)
NCATS scientists created human cell–based models of a rare disorder, NGLY1 deficiency, to learn more about the disease’s development and biology.
Genetics Experts Support Adding Hundreds of Treatable Rare Diseases to Newborn Screening
May 9, 2023 - NCATS News
- Clinical and Translational Science Awards (CTSA) Program
A study found that 88% of experts surveyed on rare diseases agreed that DNA testing to reveal treatable genetic disorders should be available for all infants. This additional screening could allow lifesaving treatments to be delivered to babies sooner.