News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
New Path for a Gene Therapy Trial at NIH for a Rare Metabolic Disease
November 19, 2024 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Our Impact on Clinical Trials
- Our Impact on Drug Discovery and Development
- Our Impact on Rare Diseases
- Platform Vector Gene Therapy (PaVe-GT)
Scientists at NCATS and other NIH institutes and centers are teaming up to advance a gene therapy treatment for MMA, a rare and potentially life-threatening genetic disorder.
Read Article
New FDA Designations May Jumpstart Gene Therapy Development
October 18, 2024 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
New FDA designations granted to NCATS for rare disease therapies provide financial incentives for companies to further develop treatments.
Read ArticleThe National Economic Burden of Rare Disease Study
April 12, 2022 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
123rd ACD Session Focuses on Maintaining Momentum
January 21, 2022 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
Gene Therapies for Rare Diseases
January 10, 2022 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Boost for NC Gene Therapy Companies – A New Rare Disease Consortium
December 20, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Gene Therapy Consortium Provides New Hope for Rare Disease Suffers
December 16, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
Platforms of Hope: Realizing the Potential of Genetic Medicines
December 1, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)