News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
New Path for a Gene Therapy Trial at NIH for a Rare Metabolic Disease
November 19, 2024 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Our Impact on Clinical Trials
- Our Impact on Drug Discovery and Development
- Our Impact on Rare Diseases
- Platform Vector Gene Therapy (PaVe-GT)
Scientists at NCATS and other NIH institutes and centers are teaming up to advance a gene therapy treatment for MMA, a rare and potentially life-threatening genetic disorder.
Read Article
New FDA Designations May Jumpstart Gene Therapy Development
October 18, 2024 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
New FDA designations granted to NCATS for rare disease therapies provide financial incentives for companies to further develop treatments.
Read ArticleThe BGTC is Working to Streamline the Development of Gene Therapies for Rare Diseases
November 23, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
FDA, NIH, and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
November 17, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
‘Bespoke Gene Therapy Consortium’ Sets Out to Enable Gene Therapies for Ultra-Rare Diseases
November 12, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Programing the Body to Make Its Own Medicine with Gene Therapy
November 5, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
Increasing Effective Gene Therapies For Rare Diseases
November 2, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Partnership to Expand Effective Gene Therapies for Rare Diseases
November 2, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)