News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
New Path for a Gene Therapy Trial at NIH for a Rare Metabolic Disease
November 19, 2024 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Our Impact on Clinical Trials
- Our Impact on Drug Discovery and Development
- Our Impact on Rare Diseases
- Platform Vector Gene Therapy (PaVe-GT)
Scientists at NCATS and other NIH institutes and centers are teaming up to advance a gene therapy treatment for MMA, a rare and potentially life-threatening genetic disorder.
Read Article
New FDA Designations May Jumpstart Gene Therapy Development
October 18, 2024 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
New FDA designations granted to NCATS for rare disease therapies provide financial incentives for companies to further develop treatments.
Read ArticleRare Disease Consortium to Focus on Optimizing AAV Gene Therapies
November 1, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
FDA, NIH, and 15 Partners Advance Gene Therapy Development in Rare Diseases
October 28, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
NIH, FDA and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
October 28, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
Pfizer, Novartis Sign on to Accelerate Gene Therapies for Rare Diseases with US Agencies
October 28, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
FDA, NIH Announce Bespoke Gene Therapy Consortium to Focus on Rare Diseases
October 28, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
FDA, NIH, and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
October 27, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)