News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
New Path for a Gene Therapy Trial at NIH for a Rare Metabolic Disease
November 19, 2024 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Our Impact on Clinical Trials
- Our Impact on Drug Discovery and Development
- Our Impact on Rare Diseases
- Platform Vector Gene Therapy (PaVe-GT)
Scientists at NCATS and other NIH institutes and centers are teaming up to advance a gene therapy treatment for MMA, a rare and potentially life-threatening genetic disorder.
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New FDA Designations May Jumpstart Gene Therapy Development
October 18, 2024 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
New FDA designations granted to NCATS for rare disease therapies provide financial incentives for companies to further develop treatments.
Read ArticleNIH, FDA and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
October 27, 2021 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
NIH, FDA and 15 private organizations partnered to create the Bespoke Gene Therapy Consortium to speed development of FDA-approved gene therapies for rare diseases.
Public-Private Partnership Launched to Accelerate Gene Therapies for Rare Diseases
October 27, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
The National Institutes of Health and U.S.
Creating a Playbook for Bespoke Gene Therapies
September 24, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
Sequencing Every Newborn’s Genome to Detect Diseases Faces Ethical and Practical Obstacles, but the United Kingdom Is Pushing Ahead with a Major Test
September 23, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
- Genetic and Rare Diseases (GARD) Information Center
A Medicxi-Backed Startup Looks to Tackle Treatment-Resistant Blood Cancers, and It's Going after AML First
June 10, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Global Genes Announces New Multimedia Series Focused on Advances in Gene Therapy and Editing, in Collaboration with the National Institutes of Health (NIH)
February 10, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
- Genetic and Rare Diseases (GARD) Information Center