News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
NIH Partnership Establishes New Gene Therapy Immunology and Standards Laboratory
April 23, 2026 - Grantee/Partner News
- Platform Vector Gene Therapy (PaVe-GT)
Transparency and Early Planning Are Key in Increasing Efficiency of Gene Therapy Development for Rare Diseases
February 26, 2026 - NCATS News
- Platform Vector Gene Therapy (PaVe-GT)
PaVe-GT scientists underscore strategy, framework and early interaction with the FDA to align preclinical and clinical efforts in AAV gene therapy translation.
Read ArticleNew Path for a Gene Therapy Trial at NIH for a Rare Metabolic Disease
November 19, 2024 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Our Impact on Clinical Trials
- Our Impact on Drug Discovery and Development
- Our Impact on Rare Diseases
- Platform Vector Gene Therapy (PaVe-GT)
Scientists at NCATS and other NIH institutes and centers are teaming up to advance a gene therapy treatment for MMA, a rare and potentially life-threatening genetic disorder.
Sharing Science at the NIH Research Festival
October 22, 2024 - Grantee/Partner News
- Our Impact on Rare Diseases
- Platform Vector Gene Therapy (PaVe-GT)
New FDA Designations May Jumpstart Gene Therapy Development
October 18, 2024 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
New FDA designations granted to NCATS for rare disease therapies provide financial incentives for companies to further develop treatments.
Automation and Standardization Will Cut Cell and Gene Therapy Production Costs
August 21, 2024 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
PJ Brooks, PhD, on Improved Newborn Screening, Non-Viral Gene Editing: New Frontiers for Neuromuscular Disease
June 17, 2024 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
ASGCT24: Translational Research Powering Potentially Transformative Therapies
May 10, 2024 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)