News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
NIH Awards More Than $15 Million to Fund Two Rare Diseases Consortia
September 25, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
Research Moves Slowly. Rare Diseases Don’t — So Patients Aren’t Waiting
June 28, 2025 - Media Coverage
- Our Impact on Rare Diseases
Easing the Burden of Rare Diseases Through Translational Science
November 12, 2024 - NCATS News
- Our Impact on Rare Diseases
NCATS Director Joni Rutter discusses how NCATS is addressing scientific and operational roadblocks that slow progress for rare diseases research and treatments.
Using AI to Improve Detection of Rare Diseases
July 16, 2024 - Grantee/Partner News
- Clinical and Translational Science Awards (CTSA) Program
At a Symposium on Rare Diseases, Smiles Were in Abundance
March 28, 2024 - Grantee/Partner News
- Our Impact on Rare Diseases
Pushing for Better Clinical Trial Design for Rare Diseases
October 17, 2023 - Grantee/Partner News
Genetics Experts Support Adding Hundreds of Treatable Rare Diseases to Newborn Screening
May 9, 2023 - NCATS News
- Clinical and Translational Science Awards (CTSA) Program
A study found that 88% of experts surveyed on rare diseases agreed that DNA testing to reveal treatable genetic disorders should be available for all infants. This additional screening could allow lifesaving treatments to be delivered to babies sooner.
NIH, FDA and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
October 27, 2021 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
NIH, FDA and 15 private organizations partnered to create the Bespoke Gene Therapy Consortium to speed development of FDA-approved gene therapies for rare diseases. The effort is co-led by NCATS and managed by FNIH.