News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Transparency and Early Planning Are Key in Increasing Efficiency of Gene Therapy Development for Rare Diseases
February 26, 2026 - NCATS News
- Platform Vector Gene Therapy (PaVe-GT)
PaVe-GT scientists underscore strategy, framework and early interaction with the FDA to align preclinical and clinical efforts in AAV gene therapy translation.
Read ArticleCures Within Reach Selected Three Clinical Trials in Rare/Ultra-Rare Diseases to Validate AI Predictions
February 25, 2026 - Grantee/Partner News
- Biomedical Data Translator (Translator)
More Than 30 Million Americans Living With Rare Diseases
February 23, 2026 - Grantee/Partner News
- Clinical and Translational Science Awards (CTSA) Program
Rare Diseases Clinical Research Network Awardees Expand the Reach of NIH Impact
February 5, 2026 - NCATS News
- Rare Diseases Clinical Research Network (RDCRN)
NIH awarded funding to 10 new and five continuing Rare Diseases Clinical Research Network (RDCRN) consortia to help address challenges in rare diseases treatment development.
NIH Awards Baylor More Than $15 Million to Fund Two Rare Diseases Consortia
September 30, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
NIH Awards More Than $15 Million to Fund Two Rare Diseases Consortia
September 25, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
Research Moves Slowly. Rare Diseases Don’t — So Patients Aren’t Waiting
June 28, 2025 - Media Coverage
- Our Impact on Rare Diseases
Easing the Burden of Rare Diseases Through Translational Science
November 12, 2024 - NCATS News
- Our Impact on Rare Diseases
NCATS Director Joni Rutter discusses how NCATS is addressing scientific and operational roadblocks that slow progress for rare diseases research and treatments.