News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Paving the Way for Ultrarare Bone Disease Treatment Trial
May 21, 2024 - NCATS News
- Our Impact on Drug Discovery and Development
- Therapeutics for Rare and Neglected Diseases (TRND)
Clinicians at the NIH Clinical Center will soon start testing an investigative drug for an ultrarare bone disease.
Read ArticleEveryLife Foundation Announces Scientific Workshop on ‘Ultra-Rare’ Diseases
May 16, 2024 - Media Coverage
- Our Impact on Rare Diseases
Human-on-a-Chip Approach Validated to Model Rare Autoimmune Disease
November 30, 2021 - Media Coverage
- Tissue Chip for Drug Screening
The BGTC is Working to Streamline the Development of Gene Therapies for Rare Diseases
November 23, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Hesperos Validates Utility of Human-on-a-Chip® Approach to Model Rare Autoimmune Disease, Myasthenia Gravis
November 22, 2021 - Grantee/Partner News
- Tissue Chip for Drug Screening
The Role of Gene Therapy in Curing Rare Diseases
November 18, 2021 - Media Coverage
FDA, NIH, and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
November 17, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
ICD Codes and Rare Diseases
November 16, 2021 - Media Coverage
- Our Impact on Rare Diseases