News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Paving the Way for Ultrarare Bone Disease Treatment Trial
May 21, 2024 - NCATS News
- Our Impact on Drug Discovery and Development
- Therapeutics for Rare and Neglected Diseases (TRND)
Clinicians at the NIH Clinical Center will soon start testing an investigative drug for an ultrarare bone disease.
Read ArticleEveryLife Foundation Announces Scientific Workshop on ‘Ultra-Rare’ Diseases
May 16, 2024 - Media Coverage
- Our Impact on Rare Diseases
‘Bespoke Gene Therapy Consortium’ Sets Out to Enable Gene Therapies for Ultra-Rare Diseases
November 12, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Watch: A Conversation on Breakthroughs in Rare Disease Diagnosis
November 4, 2021 - Media Coverage
UT Southwestern designated founding Rare Disease Center of Excellence
November 4, 2021 - Grantee/Partner News
Rare Diseases Cost 3 to 5 Times More than Common Diseases
November 3, 2021 - Media Coverage
- Genetic and Rare Diseases (GARD) Information Center
Increasing Effective Gene Therapies For Rare Diseases
November 2, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Sanford and NIH Raise Awareness on the Cost of Rare Diseases
November 2, 2021 - Grantee/Partner News
- Genetic and Rare Diseases (GARD) Information Center