News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Paving the Way for Ultrarare Bone Disease Treatment Trial
May 21, 2024 - NCATS News
- Our Impact on Drug Discovery and Development
- Therapeutics for Rare and Neglected Diseases (TRND)
Clinicians at the NIH Clinical Center will soon start testing an investigative drug for an ultrarare bone disease.
Read ArticleEveryLife Foundation Announces Scientific Workshop on ‘Ultra-Rare’ Diseases
May 16, 2024 - Media Coverage
- Our Impact on Rare Diseases
Sanford and NIH Raise Awareness on the Cost of Rare Diseases
November 2, 2021 - Grantee/Partner News
- Genetic and Rare Diseases (GARD) Information Center
Partnership to Expand Effective Gene Therapies for Rare Diseases
November 2, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
Rare Disease Research Was Advanced During COVID-19
November 2, 2021 - Media Coverage
- COVID-19
- Rare Diseases Clinical Research Network (RDCRN)
Rare Disease Consortium to Focus on Optimizing AAV Gene Therapies
November 1, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
NIH, FDA and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
October 28, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
Pfizer, Novartis Sign on to Accelerate Gene Therapies for Rare Diseases with US Agencies
October 28, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)