News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Paving the Way for Ultrarare Bone Disease Treatment Trial
May 21, 2024 - NCATS News
- Our Impact on Drug Discovery and Development
- Therapeutics for Rare and Neglected Diseases (TRND)
Clinicians at the NIH Clinical Center will soon start testing an investigative drug for an ultrarare bone disease.
Read ArticleEveryLife Foundation Announces Scientific Workshop on ‘Ultra-Rare’ Diseases
May 16, 2024 - Media Coverage
- Our Impact on Rare Diseases
FDA, NIH Announce Bespoke Gene Therapy Consortium to Focus on Rare Diseases
October 28, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
A Rare Disease Diagnosis Comes with Significant Health Care Costs, Study Shows
October 28, 2021 - Media Coverage
- Our Impact on Rare Diseases
FDA, NIH, and 15 Partners Advance Gene Therapy Development in Rare Diseases
October 28, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
NIH, FDA and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
October 27, 2021 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
NIH, FDA and 15 private organizations partnered to create the Bespoke Gene Therapy Consortium to speed development of FDA-approved gene therapies for rare diseases.
Public-Private Partnership Launched to Accelerate Gene Therapies for Rare Diseases
October 27, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
The National Institutes of Health and U.S.
FDA, NIH, and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
October 27, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)