News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Paving the Way for Ultrarare Bone Disease Treatment Trial
May 21, 2024 - NCATS News
- Our Impact on Drug Discovery and Development
- Therapeutics for Rare and Neglected Diseases (TRND)
Clinicians at the NIH Clinical Center will soon start testing an investigative drug for an ultrarare bone disease.
Read ArticleEveryLife Foundation Announces Scientific Workshop on ‘Ultra-Rare’ Diseases
May 16, 2024 - Media Coverage
- Our Impact on Rare Diseases
Genetic Analysis Suggests Dilated Cardiomyopathy Therapies May Work for Rare Peripartum Cardiomyopathy
May 11, 2021 - NCATS News
- Clinical and Translational Science Awards (CTSA) Program
Analyzing genetic information drawn from patients and multiple databases, CTSA Program researchers discovered similarities between nonischemic dilated cardiomyopathy (DCM) and peripartum cardiomyop
Kyowa Kirin Receives Positive CHMP Opinion for the Self-Administration of CRYSVITA® ▼ (burosumab) to Treat X-Linked Hypophosphataemia (XLH), a Rare Metabolic Bone Disorder
May 10, 2021 - Grantee/Partner News
- Genetic and Rare Diseases (GARD) Information Center
A Ray of Hope for a Rare and Deadly Skin Cancer
May 4, 2021 - Grantee/Partner News
- Our Impact on Drug Discovery and Development
AllStripes Announces Collaboration with NIH’s NCATS to Launch Effort in Rare Disease Diagnosis
April 27, 2021 - Grantee/Partner News
- Genetic and Rare Diseases (GARD) Information Center
2021 Rare Disease Day at NIH: Finding Hope Within Uncertainty
April 1, 2021 - NCATS News
The COVID-19 pandemic has profoundly affected nearly every aspect of the rare disease world.
FDA to Focus on Patients with Rare Diseases
April 1, 2021 - Grantee/Partner News