TRND Clinical Research Studies

For more details about clinical research studies supported by TRND, click on the links below or visit ClinicalTrials.gov.

Active Studies

Creatine Transporter Deficiency

GNE Myopathy (previously known at Hereditary Inclusion Body Myopathy)

Niemann-Pick Disease Type C

Completed Studies

Chronic Lymphocytic Leukemia

GNE Myopathy (previously known at Hereditary Inclusion Body Myopathy)

Niemann-Pick Disease Type C1