News & Events

Read our latest research news, explore upcoming events and find resources describing our mission and programs.

Latest News

NCATS Stories

Baby KJ sits on Nicole Muldoon’s lap while Dr. Rebecca Ahrens-Nicklas hold a microphone up to them.

Rare Disease Day at NIH 2026: Paving the Way to a Brighter Future for All Americans

March 31, 2026 - NCATS News

Our Impact on Rare Diseases

The rare diseases community came together at the NIH Natcher Conference Center and virtually to celebrate Rare Disease Day at NIH, highlighting inspiring stories, impactful research advances, and new possibilities for the future.

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DNA double-helix with ribbons attached that read "Preclinical" and "Regulatory"

Transparency and Early Planning Are Key in Increasing Efficiency of Gene Therapy Development for Rare Diseases

February 26, 2026 - NCATS News

Platform Vector Gene Therapy (PaVe-GT)

PaVe-GT scientists underscore strategy, framework and early interaction with the FDA to align preclinical and clinical efforts in AAV gene therapy translation.

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Partner & Grantee News

New FDA Plausible Mechanism Framework Spurs Development of Personalized In Vivo Prime Editing Platform for Urea Cycle Disorders

March 31, 2026 - Grantee/Partner News

Somatic Cell Genome Editing (SCGE)

By Finding ‘Bright Spots’ in the Opioid Crisis, VCU Researchers Are Mapping a Path to Better Outcomes

March 23, 2026 - Grantee/Partner News

Clinical and Translational Science Awards (CTSA) Program

Tool May Identify More Patients Who Could Benefit From Parathyroid Surgery

March 19, 2026 - Grantee/Partner News

Our Impact on Tools and Technologies

Upcoming Events

Advisory Council Meeting: May 2026

May 21, 2026 - May 22, 2026 - Advisory Board

The NCATS Advisory Council will convene a virtual/in-person meeting on May 21–22, 2026. The meeting will feature presentations from NCATS Director Joni L. Rutter, Ph.D., and others about the center’s initiatives, policies, programs and future direction.

Location: TBD
Open Session: Time TBD

Publications

Browse a listing of peer-reviewed scientific publications that feature research supported by NCATS programs and initiatives.

A Systematic Review and Meta-Analysis of Breast Arterial Calcification and Its Association With Cardiovascular Disease and All-Cause Mortality

Clinical and Translational Science Awards (CTSA) Program - April 15, 2026 - The American Journal of Cardiology

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TFEB Degradation Is Regulated by an IKK/β-TrCP2 Phosphorylation-Ubiquitination Cascade

Clinical and Translational Science Awards (CTSA) Program - April 1, 2026 - Nature Communications