News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Paving the Way for Ultrarare Bone Disease Treatment Trial
May 21, 2024 - NCATS News
- Our Impact on Drug Discovery and Development
- Therapeutics for Rare and Neglected Diseases (TRND)
Clinicians at the NIH Clinical Center will soon start testing an investigative drug for an ultrarare bone disease.
Read ArticleEveryLife Foundation Announces Scientific Workshop on ‘Ultra-Rare’ Diseases
May 16, 2024 - Media Coverage
- Our Impact on Rare Diseases
Boost for NC Gene Therapy Companies – A New Rare Disease Consortium
December 20, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Dr. Anne Pariser Provides an Overview of NIH’s Office of Rare Diseases Research
December 20, 2021 - Media Coverage
Gene Therapy Consortium Provides New Hope for Rare Disease Suffers
December 16, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
Not So Rare Diseases: The Cumulative Burden of Underdiagnosis
December 14, 2021 - Media Coverage
NCATS’ Office of Rare Diseases Research Director Anne R.
Dr Anne Pariser Provides an Overview of NIH’s Office of Rare Diseases Research
December 1, 2021 - Media Coverage
Drug Repurposing Approaches Reveal HIV Drug Holds Promise Against a Rare, Disabling Muscle Disorder
November 30, 2021 - NCATS News
Using drug repurposing approaches, researchers from NCATS, Duke University and the University of Florida discovered that an existing antiviral drug used against HIV infection may be helpful in trea