News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Paving the Way for Ultrarare Bone Disease Treatment Trial
May 21, 2024 - NCATS News
- Our Impact on Drug Discovery and Development
- Therapeutics for Rare and Neglected Diseases (TRND)
Clinicians at the NIH Clinical Center will soon start testing an investigative drug for an ultrarare bone disease.
Read ArticleEveryLife Foundation Announces Scientific Workshop on ‘Ultra-Rare’ Diseases
May 16, 2024 - Media Coverage
- Our Impact on Rare Diseases
Cost of Rare Diseases in US? Nearly $1 Trillion in 2019, EveryLife Foundation Finds
March 30, 2021 - Media Coverage
- Genetic and Rare Diseases (GARD) Information Center
NCATS Researchers’ New Approach to Measure Gene Activity Could Speed Search for Rare Disease Therapies
March 23, 2021 - NCATS News
- Our Impact on Research Operations
NCATS scientists design an innovative test to find potential treatments for Charcot-Marie-Tooth disease (CMT), one of the most common inherited neurological diseases, opening new pathways for rare
COVID's All-Hands-on-Deck Approach Should Be Standard for Rare Diseases
March 18, 2021 - Media Coverage
- COVID-19
Pandemic Perspectives: US FDA, NIH Tried to Be Flexible to Keep Rare Disease Trials Going
March 9, 2021 - Media Coverage
- COVID-19
How Covid-19 Is Changing Rare Diseases Research
March 9, 2021 - Media Coverage
- COVID-19
Twenty years after researchers published their first discoveries associated with human genome sequencing, policymakers are fighting to overcome obstacles that hobble the potential of genetic medici
Pandemic Perspectives: NCATS Director Urges Rare Disease Community to Push against Return to Clinical Trial Status Quo
March 9, 2021 - Media Coverage
- COVID-19