News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Yale Co-Leads New National Consortium for Rare Skin Disorders
October 12, 2026 - Grantee/Partner News
- Our Impact on Rare Diseases
- Rare Diseases Clinical Research Network (RDCRN)
$7.6M NIH Grant Will Accelerate Study, Treatment for Rare Genetic and Developmental Disorders in Children
September 28, 2026 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
NIH, AlphaRose Study Advances Personalised Therapy Approach for Rare Genetic Disorder
July 16, 2026 - Media Coverage
- Our Impact on Drug Discovery and Development
- Our Impact on Rare Diseases
FDA OKs First-in-Human Trial for BGTC-Supported Rare Disease Gene Therapy
July 7, 2026 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
AI-Guided Pathology Analysis Can Help Predict Immunotherapy Response in Rare Cancers
June 30, 2026 - Grantee/Partner News
- Clinical and Translational Science Awards (CTSA) Program
How Repurposing a Drug May Help Treat More Rare Gastrointestinal Diseases
June 29, 2026 - NCATS News
- Rare Diseases Clinical Research Network (RDCRN)
RDCRN researchers found that dupilumab — a drug used for asthma and chronic obstructive pulmonary disease — shows promise in treating eosinophilic gastritis.
FDA Clears IND for Gene Therapy Candidate to Treat Rare Metabolic Disorder
May 21, 2026 - NCATS News
- Our Impact on Clinical Trials
- Our Impact on Drug Discovery and Development
- Our Impact on Rare Diseases
MMA-101, an NIH-supported AAV gene therapy for a rare metabolic disorder, has received FDA clearance to begin clinical testing.
WEST AI Algorithm May Help Speed Diagnosis of Rare Diseases
April 14, 2026 - NCATS News
- Clinical and Translational Science Awards (CTSA) Program
- Our Impact on Rare Diseases
Rare diseases can take years to diagnose. WEST — a new AI algorithm — aims to cut that diagnostic odyssey by learning from complete and incomplete real-world EHR data.