News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Transparency and Early Planning Are Key in Increasing Efficiency of Gene Therapy Development for Rare Diseases
February 26, 2026 - NCATS News
- Platform Vector Gene Therapy (PaVe-GT)
PaVe-GT scientists underscore strategy, framework and early interaction with the FDA to align preclinical and clinical efforts in AAV gene therapy translation.
Read ArticleCures Within Reach Selected Three Clinical Trials in Rare/Ultra-Rare Diseases to Validate AI Predictions
February 25, 2026 - Grantee/Partner News
- Biomedical Data Translator (Translator)
Working Together Is the Name of the Game at Rare Disease Day at NIH 2019
April 4, 2019 - NCATS News
Rare Disease Day at NIH, held on February 28, 2019, exemplifies NCATS’ approach to rare diseases research: involving patients as partners throughout the translational research process to ensure that research and interventions address patients’ needs.
New Method Could Help Find Potential Treatments for Rare Diseases
January 5, 2019 - NCATS News
- Preclinical Chemical Biology Laboratory
Scientists in NCATS’ Assay Development and Screening Technology Program are developing new methods for screening small molecules that could help researchers test possible drugs and develop new treatments for many diseases.