News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Paving the Way for Ultrarare Bone Disease Treatment Trial
May 21, 2024 - NCATS News
- Our Impact on Drug Discovery and Development
- Therapeutics for Rare and Neglected Diseases (TRND)
Clinicians at the NIH Clinical Center will soon start testing an investigative drug for an ultrarare bone disease.
Read ArticleEveryLife Foundation Announces Scientific Workshop on ‘Ultra-Rare’ Diseases
May 16, 2024 - Media Coverage
- Our Impact on Rare Diseases
Researchers Create 3-D Model for Rare Neuromuscular Disorders, Setting Stage for Clinical Trial
April 20, 2022 - Media Coverage
- Small Business (SBIR)
- Tissue Chip for Drug Screening
Hesperos Shows Potential for In Vitro Approach to Replace Conventional Animal Efficacy Studies for Rare Neuromuscular Disorders
April 19, 2022 - Grantee/Partner News
- Small Business (SBIR)
- Tissue Chip for Drug Screening
Researchers Create 3-D Model for Rare Neuromuscular Disorders, Setting Stage for Clinical Trial
April 19, 2022 - NCATS News
- Small Business (SBIR)
- Tissue Chip for Drug Screening
Partially funded by a Small Business Innovation Research grant from NCATS, Hesperos, Inc., researchers created a tissue chip model that mimics the biology of two rare neuromuscular disorders, setti
NCATS Aims to Transform Rare Disease Research
April 15, 2022 - Grantee/Partner News
- Our Impact on Rare Diseases
The National Economic Burden of Rare Disease Study
April 12, 2022 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
Examining the Burden of Rare Diseases in the US
March 31, 2022 - Media Coverage
- Genetic and Rare Diseases (GARD) Information Center