News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
How Repurposing a Drug May Help Treat More Rare Gastrointestinal Diseases
June 29, 2026 - NCATS News
- Rare Diseases Clinical Research Network (RDCRN)
RDCRN researchers found that dupilumab — a drug used for asthma and chronic obstructive pulmonary disease — shows promise in treating eosinophilic gastritis.
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FDA Clears IND for Gene Therapy Candidate to Treat Rare Metabolic Disorder
May 21, 2026 - NCATS News
- Our Impact on Clinical Trials
- Our Impact on Drug Discovery and Development
- Our Impact on Rare Diseases
MMA-101, an NIH-supported AAV gene therapy for a rare metabolic disorder, has received FDA clearance to begin clinical testing.
Read ArticleNIH Awards More Than $15 Million to Fund Two Rare Diseases Consortia
September 25, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
NIH Awards $8.6 Million Grant to Renew Rare Disease Clinical Research Network for Neurodevelopmental Studies
September 15, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
Gene Editing Reverses Symptoms of Rare Brain Disorder in Mice
July 22, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
Genome Editing Corrected Rare Brain Mutations in Mice. Could It Help Fight Neurological Diseases?
July 21, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
Experimental Compound Offers Potential Treatment for Rare, Often Fatal, Childhood Disease
July 9, 2025 - Grantee/Partner News
- Clinical and Translational Science Awards (CTSA) Program
Research Moves Slowly. Rare Diseases Don’t — So Patients Aren’t Waiting
June 28, 2025 - Media Coverage
- Our Impact on Rare Diseases