News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
NIH, AlphaRose Study Advances Personalised Therapy Approach for Rare Genetic Disorder
July 16, 2026 - Media Coverage
- Our Impact on Drug Discovery and Development
- Our Impact on Rare Diseases
FDA OKs First-in-Human Trial for BGTC-Supported Rare Disease Gene Therapy
July 7, 2026 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
A Rare Respiratory Disease May Be More Prevalent in Quebec
November 27, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
NIH Awards Baylor More Than $15 Million to Fund Two Rare Diseases Consortia
September 30, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
NIH Awards $15M+ to Baylor-Led Consortia Targeting Rare Bone and Metabolic Disorders
September 27, 2025 - Media Coverage
- Rare Diseases Clinical Research Network (RDCRN)
NIH Awards More Than $15 Million to Fund Two Rare Diseases Consortia
September 25, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
NIH Awards $8.6 Million Grant to Renew Rare Disease Clinical Research Network for Neurodevelopmental Studies
September 15, 2025 - Grantee/Partner News
- Rare Diseases Clinical Research Network (RDCRN)
Gene Editing Reverses Symptoms of Rare Brain Disorder in Mice
July 22, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)