News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
Medical Miracles at Penn Medicine: Breakthrough With Customized CRISPR Treatment for Patient With CPS1
December 16, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
Mapping ‘Dark’ Regions of the Genome Illuminates How Cells Respond to Their Environment
September 25, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
Research Spotlight: Laying the Foundation for Gene Editing for Inherited Progressive Deafness in Adults, DFNA41
August 14, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
Gene Editing Reverses Symptoms of Rare Brain Disorder in Mice
July 22, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
Genome Editing Corrected Rare Brain Mutations in Mice. Could It Help Fight Neurological Diseases?
July 21, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
A Gene Editing First Augurs an Era of Bespoke Therapies
June 12, 2025 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
Cell and Gene Therapy Leaders Tell FDA: “Believe in American Solutions”
June 5, 2025 - Media Coverage
- Somatic Cell Genome Editing (SCGE)
Infant with Rare, Incurable Disease is First to Successfully Receive Personalized Gene Therapy Treatment
May 28, 2025 - NCATS News
- Our Impact on Rare Diseases
- Somatic Cell Genome Editing (SCGE)
NIH-supported gene-editing platform lays groundwork to rapidly develop treatments for other rare genetic diseases.