Skip to main content

News

Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.

News

Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.

New FDA Plausible Mechanism Framework Spurs Development of Personalized In Vivo Prime Editing Platform for Urea Cycle Disorders

March 31, 2026 - Grantee/Partner News

  • Somatic Cell Genome Editing (SCGE)

Transparency and Early Planning Are Key in Increasing Efficiency of Gene Therapy Development for Rare Diseases

February 26, 2026 - NCATS News

  • Platform Vector Gene Therapy (PaVe-GT)

PaVe-GT scientists underscore strategy, framework and early interaction with the FDA to align preclinical and clinical efforts in AAV gene therapy translation.

Children’s Hospital of Philadelphia Marks One-Year Anniversary of World’s First Personalized CRISPR Gene Therapy for Child with Rare Genetic Disease

February 24, 2026 - Grantee/Partner News

  • Somatic Cell Genome Editing (SCGE)

Medical Miracles at Penn Medicine: Breakthrough With Customized CRISPR Treatment for Patient With CPS1

December 16, 2025 - Grantee/Partner News

  • Somatic Cell Genome Editing (SCGE)

Mapping ‘Dark’ Regions of the Genome Illuminates How Cells Respond to Their Environment

September 25, 2025 - Grantee/Partner News

  • Somatic Cell Genome Editing (SCGE)

Research Spotlight: Laying the Foundation for Gene Editing for Inherited Progressive Deafness in Adults, DFNA41

August 14, 2025 - Grantee/Partner News

  • Somatic Cell Genome Editing (SCGE)

Last updated on March 31, 2026