News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
“It Was Not a Cure”: Musunuru Cautions ASGCT on Baby KJ Promise
May 13, 2026 - Media Coverage
- Somatic Cell Genome Editing (SCGE)
NIH Partnership Establishes New Gene Therapy Immunology and Standards Laboratory
April 23, 2026 - Grantee/Partner News
- Platform Vector Gene Therapy (PaVe-GT)
New FDA Plausible Mechanism Framework Spurs Development of Personalized In Vivo Prime Editing Platform for Urea Cycle Disorders
March 31, 2026 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
Transparency and Early Planning Are Key in Increasing Efficiency of Gene Therapy Development for Rare Diseases
February 26, 2026 - NCATS News
- Platform Vector Gene Therapy (PaVe-GT)
PaVe-GT scientists underscore strategy, framework and early interaction with the FDA to align preclinical and clinical efforts in AAV gene therapy translation.
Children’s Hospital of Philadelphia Marks One-Year Anniversary of World’s First Personalized CRISPR Gene Therapy for Child with Rare Genetic Disease
February 24, 2026 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
Medical Miracles at Penn Medicine: Breakthrough With Customized CRISPR Treatment for Patient With CPS1
December 16, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
Mapping ‘Dark’ Regions of the Genome Illuminates How Cells Respond to Their Environment
September 25, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)
Research Spotlight: Laying the Foundation for Gene Editing for Inherited Progressive Deafness in Adults, DFNA41
August 14, 2025 - Grantee/Partner News
- Somatic Cell Genome Editing (SCGE)