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News

Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.

News

Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.

Gene Therapy: The Future Made Present for Addressing Rare Diseases

April 18, 2023 - Media Coverage

  • Bespoke Gene Therapy Consortium (BGTC)

NIH, FDA and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases

October 27, 2021 - NCATS News

  • Bespoke Gene Therapy Consortium (BGTC)
  • Platform Vector Gene Therapy (PaVe-GT)

NIH, FDA and 15 private organizations partnered to create the Bespoke Gene Therapy Consortium to speed development of FDA-approved gene therapies for rare diseases. The effort is co-led by NCATS and managed by FNIH.

NIH Study Suggests People with Rare Diseases Face Significantly Higher Health Care Costs

October 22, 2021 - NCATS News

Results from a collaborative pilot study suggest health care costs for each person with a rare disease are three to five times greater than the costs for those who do not have a rare disease.

New Method Could Help Find Potential Treatments for Rare Diseases

January 5, 2019 - NCATS News

  • Preclinical Chemical Biology Laboratory

Scientists in NCATS’ Assay Development and Screening Technology Program are developing new methods for screening small molecules that could help researchers test possible drugs and develop new treatments for many diseases.

Last updated on September 8, 2025